


Searching News Database: porphyria
HSMN NewsFeed - 6 Jul 2016
US FDA pathway opens to SCENESSE(R) following Fast Track designation for treatment of EPP
US FDA pathway opens to SCENESSE(R) following Fast Track designation for treatment of EPP
HSMN NewsFeed - 13 Jan 2014
Alnylam and Genzyme Form Transformational Alliance for RNAi Therapeutics as Genetic Medicines
Alnylam and Genzyme Form Transformational Alliance for RNAi Therapeutics as Genetic Medicines
HSMN NewsFeed - 20 Jul 2012
First Gene Therapy in Western World Receives Positive Opinion in Europe from CHMP
First Gene Therapy in Western World Receives Positive Opinion in Europe from CHMP
HSMN NewsFeed - 4 Jan 2012
Amsterdam Molecular Therapeutics Receives US Orphan Designation for Hemophilia B Gene Therapy
Amsterdam Molecular Therapeutics Receives US Orphan Designation for Hemophilia B Gene Therapy
HSMN NewsFeed - 8 Jul 2011
Amsterdam Molecular Therapeutics Files Glybera(R) European Marketing Application for Re-examination
Amsterdam Molecular Therapeutics Files Glybera(R) European Marketing Application for Re-examination
HSMN NewsFeed - 24 Jun 2011
Amsterdam Molecular Therapeutics Receives Opinion on Glybera(R) Marketing Authorisation Application
Amsterdam Molecular Therapeutics Receives Opinion on Glybera(R) Marketing Authorisation Application
HSMN NewsFeed - 12 Mar 2007
New European Approval for Xyrem(R) Provides Significant Advance in the Treatment of Narcolepsy
New European Approval for Xyrem(R) Provides Significant Advance in the Treatment of Narcolepsy
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